CRISPR–Cas9 hits its target in amyloidosis. Read the latest clinical trial analysis in The Clinical Pipeline, from CyrilPedia
have announced interim results
from the cardiomyopathy arm of their phase 1 trial for transthyretin amyloidosis. Patients treated with their CRISPR–Cas9-based gene-editing treatment, NTLA-2001, showed a dramatic reduction in levels of serum transthyretin . The announcement followed positive data published last year in from the hereditary polyneuropathy arm of the same trial. NTLA-2001 showed a good safety profile in both arms, but data on clinical efficacy are not yet available for either.
Deutschland Neuesten Nachrichten, Deutschland Schlagzeilen
Similar News:Sie können auch ähnliche Nachrichten wie diese lesen, die wir aus anderen Nachrichtenquellen gesammelt haben.
Health effects associated with vegetable consumption: a Burden of Proof study - Nature MedicineA meta-analysis using the Burden of Proof function identified modest evidence supporting a protective role of vegetable consumption and ischemicheartdisease, stroke and esophageal cancer, but not type 2 diabetes. IHME_UW
Weiterlesen »
Health effects associated with smoking: a Burden of Proof study - Nature MedicineA meta-analysis using the Burden of Proof method reported consistent evidence supporting harmful associations between smoking and 28 different health outcomes. IHME_UW
Weiterlesen »
How COVID-19 shaped mental health: from infection to pandemic effects - Nature MedicineThis Review discusses the impact of COVID-19 on mental health, from pandemic-related societal effects to direct infection-related neuropsychiatric sequelae, highlighting the lessons learned and outstanding knowledge gaps.
Weiterlesen »
Systolic blood pressure and cardiovascular health - Nature MedicineNew analyses are prompting a shift in how we think about systolic blood pressure, with substantial benefits to be gained from population-wide interventions alongside targeting high-risk groups.
Weiterlesen »
Africa must participate in finding a gene therapy cure for sickle-cell disease - Nature MedicineAfrica must participate in finding a gene therapy cure for sickle-cell disease. Correspondence from juliemakani and colleagues muhimbiliuniver
Weiterlesen »
Shining a light on the psychological burden of cancer - Nature MedicineTo raise awareness of WorldMentalHealthDay here is the accompanying News and Views article highlighting the psychological burden of cancer WMHDay
Weiterlesen »